A Sequential Dose-Escalation, Randomized, Active-Controlled, Multi-Center, Phase 1/2a Clinical Trial to Evaluate the Safety, Tolerability and Efficacy of SNR1611 in Patients With Amyotrophic Lateral Sclerosis

Study Purpose:

The purpose of this study is to evaluate the safety, tolerability and efficacy of trametinib (SNR1611) in the treatment of amyotrophic lateral sclerosis.

Study Status:

Not recruiting

Disease:

Amyotrophic Lateral Sclerosis

Study Type:

Interventional

Type of Intervention:

Drug

Intervention Name:

Trametinib (0.5 mg), Trametinib (1 mg), Riluzole (100 mg)

Placebo:

No

Phase:

Phase 1/Phase 2

Study Chair(s)/Principal Investigator(s):

Byoung Joon Kim, Samsung Medical Center, Seoul, Republic of Korea

Clinicaltrials.gov ID:

NCT04326283

Neals Affiliated?

No

Coordinating Center Contact Information

Full Study Summary:

Trametinib (SNR1611) is a MEK inhibitor that downregulates the MAPK/ERK pathway. In this study, the potential of MAPK/ERK pathway downregulation through trametinib (SNR1611) as a therapeutic treatment for amyotrophic lateral sclerosis (ALS) will be evaluated.

Study Sponsor:

Genuv Inc.

Estimated Enrollment:

23

Estimated Study Start Date:

04 / 02 / 2020

Estimated Study Completion Date:

04 / 28 / 2023

Posting Last Modified Date:

05 / 09 / 2023

Date Study Added to neals.org:

03 / 30 / 2020

Minimum Age:

19 Years

Maximum Age:

75 Years

Main inclusion criteria:

- Patients diagnosed as definite, probable or probable-laboratory-supported ALS according to El Escorial Criteria.

- Patients of less than 2 years after the onset of ALS.

- Patients who meet the criteria of K-ALSFRS-R score and forced vital capacity.

Main exclusion criteria:

- Patients with primary lateral sclerosis, progressive muscular atrophy or lower motor neuron disease.

- Patients who have history of ALS treatment of edaravone or stem cell therapy within 16 weeks before screening.

- Patients who have permanently ceased the administration of riluzole due to lack of tolerability and/or efficacy.

- Patients in Class II to IV according to the New York Heart Association functional classification. Patients with myocardial infarction, unstable arrhythmia, and/or significant cardiovascular disease such as unstable angina within 12 weeks before screening.

- Patients who do not meet the criteria of laboratory tests and medical/operation history.

Inje University Busan Paik Hospital

Busan
Korea, Republic of

Asan Medical Center

Seoul
Korea, Republic of

Korea University Anam Hospital

Seoul
Korea, Republic of

Samsung Medical Center

Seoul
Korea, Republic of

Severance Hospital, Yonsei University Health System

Seoul
Korea, Republic of